Search Results

Safety and Efficacy of IL-12 Plasmid DNA Transfection into Pig Skin: Supportive Data for Human Clinical Trials on Gene Therapy and Vaccination.

• Authors : Lampreht Tratar, Ursa; Jesenko, Tanja; Omerzel, Masa

Subjects: GENE therapy; CLINICAL trials; DNA vaccines

• Source: International Journal of Molecular Sciences; Mar2024, Vol. 25 Issue 6, p3151, 12p

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Recent developments in gene therapy research in India.

• Authors : Selot, Ruchita; Ghosh, Arkasubhra

• Source: Journal of Biosciences; Mar2024, Vol. 49 Issue 1, p1-26, 26p

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Gene Therapy for Genetic Syndromes: Understanding the Current State to Guide Future Care.

• Authors : Henderson, Marian L.; Zieba, Jacob K.; Li, Xiaopeng

Subjects: GENE therapy; SPINAL muscular atrophy; DUCHENNE muscular dystrophy

• Source: BioTech; Mar2024, Vol. 13 Issue 1, p1, 31p

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Gene therapy for adenosine deaminase severe combined immune deficiency—An unexpected journey of four decades.

• Authors : Kohn, Donald B.

Subjects: ADENOSINE deaminase; GENE therapy; IMMUNODEFICIENCYEUROPEAN Union; EUROPEAN Medicines Agency

• Source: Immunological Reviews; Mar2024, Vol. 322 Issue 1, p148-156, 9p

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Update: Gene therapy clinical trials in neovascular age-related macular degeneration: Companies are attacking the disease from multiple angles.

• Authors : Rowe, Lucas W.; Ciulla, Thomas A.

Subjects: VASCULAR endothelial growth factor antagonists; THERAPEUTIC use of monoclonal antibodies; GENE therapy

• Source: Retina Specialist; Mar/Apr2024, Vol. 9, p22-26, 5p

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Navigating Gene Therapy Access: The Case of Bulgaria in the Context of the EU Regulatory Landscape.

• Authors : Kostadinov, Kostadin; Marinova, Yuliyana; Dimitrov, Kostadin

Subjects: HEALTH services accessibility; RESEARCH methodology; UNCERTAINTYBULGARIAEUROPEAN Union

• Source: Healthcare (2227-9032); Feb2024, Vol. 12 Issue 4, p458, 13p

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AAV-RPGR Gene Therapy Rescues Opsin Mislocalisation in a Human Retinal Organoid Model of RPGR -Associated X-Linked Retinitis Pigmentosa.

• Authors : Sladen, Paul E.; Naeem, Arifa; Adefila-Ideozu, Toyin

Subjects: RETINITIS pigmentosa; GENE therapy; CLINICAL trials

• Source: International Journal of Molecular Sciences; Feb2024, Vol. 25 Issue 3, p1839, 14p

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Gene therapy for glycogen storage diseases.

• Authors : Koeberl, Dwight D.; Koch, Rebecca L.; Lim, Jeong‐A.

• Source: Journal of Inherited Metabolic Disease; Jan2024, Vol. 47 Issue 1, p93-118, 26p

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Redefining informed consent form in cell and gene therapy trials.

• Authors : Dalal, Varsha; Jotwani, Geeta; Yadav, Munna Lal

Subjects: GENE therapy; CELLULAR therapy; MEDICAL ethicsINDIA

• Source: Perspectives in Clinical Research; Jan-Mar2024, Vol. 15 Issue 1, p4-9, 6p

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Gene therapy for haemophilia A and B, from basic principles to clinical implementation: An illustrated review.

• Authors : Ay, Cihan; Frenzel, Laurent; Pinachyan, Karen

Subjects: GENE therapy; HEMOPHILIA; CLINICAL trials

• Source: Haemophilia; Jan2024, Vol. 30 Issue 1, p5-15, 11p

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